The number of people with the condition has increased rapidly in recent decades. Some researchers and clinicians worry that ...

Autism is diagnosed more often in boys than in girls. Part of the reason might be that girls are more difficult to diagnose.

A new nonprofit wants to streamline gene therapy for diseases often avoided by pharmaceutical companies — making treatment more like a routine procedure than a bespoke drug.

The findings may one day pave the way for scientists to design treatments that allow these phases of brain development to ...

While some research has shown benefits for patients who qualify, questions remain about the therapy's long-term risks and use among men without a medical need.

Some side effects of antipsychotics may not appear until years after treatment begins, making long-term monitoring an essential part of care.

Gregory Maassen was nearly bedridden by a burning sensation that was later diagnosed as a rare form of neuropathy. He has ...

RAG-17 is an experimental RNA-targeting therapy designed to lower toxic SOD1 protein in people with SOD1-ALS. A six-person trial found RAG-17 was well tolerated, with no serious side effects. RAG-17 ...

The Food and Drug Administration has approved a first-of-its-kind pill that can drastically reduce cholesterol in a way that's previously only been ...